Pipeline — registered trials by phase
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy
— · Duchenne Muscular Dystrophy · Enrolling By Invitation · est. 2029-12-31
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice
— · Duchenne Muscular Dystrophy · Enrolling By Invitation · est. 2033-12-31
A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice
— · Limb-girdle Muscular Dystrophy · Active Not Recruiting · est. 2030-09-05
Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting
— · Duchenne Muscular Dystrophy · Recruiting · est. 2027-08-31
Pharmacokinetic Study of a Single Dose of AVI-4126 (RESTEN-NG®) in Cerebral Spinal Fluid
— · Neoplasms · Completed · est. 2006-06
Pharmacokinetic Study in Cerebral Spinal Fluid After a Single Dose of AVI-4020
— · West Nile Virus · Completed · est. 2006-12
A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirsen) in Patients With Duchenne Muscular Dystrophy (DMD)
— · Muscular Dystrophy, Duchenne · Completed · est. 2019-08-19
Pharmacokinetic Study of a Single Dose of AVI-4065 in Cerebral Spinal Fluid
— · Encephalitis · Completed · est. 2006-10
Safety Study of Single Administration Post-exposure Prophylaxis Treatment for Marburg Virus
— · Marburg Hemorrhagic Fever · Completed · est. 2011-12
Safety Study of Single Administration Post-Exposure Prophylaxis Treatment for Ebola Virus
— · Ebola Hemorrhagic Fever · Completed · est. 2011-11
Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patients
— · Duchenne Muscular Dystrophy · Completed · est. 2018-10-03
A Study to Assess the Safety, Tolerability and Pharmacokinetics of AVI-7288 in Healthy Adult Volunteers
— · Marburg Hemorrhagic Fever · Completed · est. 2014-01
A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulatory and Ambulatory Participants With Limb Girdle Muscular Dystrophy, Type 2E/R4 (Beta-Sarcoglycan [β-SG] Deficiency)
— · Limb Girdle Muscular Dystrophy · Active Not Recruiting · est. 2028-08-28
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
— · Duchenne Muscular Dystrophy · Recruiting · est. 2027-12-31
rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
— · Dysferlinopathy · Completed · est. 2019-07
A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's Disease
— · Huntington's Disease · Recruiting · est. 2027-11-30
Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy
— · Muscular Dystrophy, Duchenne · Completed · est. 2017-04-21
Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) Patients
— · Duchenne Muscular Dystrophy · Completed · est. 2010-06
Phase I/II Study of SRP-4053 in DMD Patients
— · Duchenne Muscular Dystrophy · Completed · est. 2019-03-25
Safety and Efficacy of RESTEN-MP When Used in Conjunction With a Bare Metal Stent in Coronary Arteries
— · Coronary Artery Disease, Coronary Restenosis · Completed
A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
— · Duchenne Muscular Dystrophy · Completed · est. 2023-04-25
Study of SRP-1003 in Participants With Type 1 Myotonic Dystrophy
— · Myotonic Dystrophy 1 · Enrolling By Invitation · est. 2026-12-31
Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy
— · Duchenne Muscular Dystrophy (DMD) · Completed · est. 2016-04-15
Study of SRP-1001 in Adult and Adolescent Participants With Facioscapulohumeral Muscular Dystrophy Type 1
— · Muscular Dystrophy, Facioscapulohumeral · Enrolling By Invitation · est. 2028-12-31
Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skipping
— · Duchenne Muscular Dystrophy · Completed · est. 2021-03-10
A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne Muscular Dystrophy (DMD)
— · Muscular Dystrophy, Duchenne · Completed · est. 2020-12-08
Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients
— · Duchenne Muscular Dystrophy · Completed · est. 2012-02
Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy
— · Duchenne Muscular Dystrophy (DMD) · Completed · est. 2018-12-17
A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants With Limb-Girdle Muscular Dystrophy, Type 2D (LGMD2D)
— · Limb-Girdle Muscular Dystrophy, Type 2D · Completed · est. 2019-03-14
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
— · Duchenne Muscular Dystrophy · Active Not Recruiting · est. 2027-05-31
Study of Eteplirsen in DMD Patients
— · Duchenne Muscular Dystrophy (DMD) · Completed · est. 2019-06-14
A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON)
— · Muscular Dystrophy, Duchenne · Active Not Recruiting · est. 2026-10-31
Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD)
— · Duchenne Muscular Dystrophy · Completed · est. 2024-11-12
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
— · Limb-girdle Muscular Dystrophy · Active Not Recruiting · est. 2025-03-04
A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
— · Duchenne Muscular Dystrophy · Enrolling By Invitation · est. 2033-10-31
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)
— · Duchenne Muscular Dystrophy · Completed · est. 2023-10-04
No approved products listed under this sponsor in Drugs@FDA (partnered or subsidiary products may be listed elsewhere).
Source: ClinicalTrials.gov (trials where Sarepta is lead sponsor; 36 active or completed) and Drugs@FDA (0 approved products). Registry data can include older or partnered programs; the company's own pipeline page is the official list.
SEC filings — insider trading forms excluded
- 8-K2026-09-23Current report (material event)
- 13F-HR2026-08-1413F-HR
- SCHEDULE 13G/A2026-08-13SCHEDULE 13G/A
- SCHEDULE 13G2026-08-07SCHEDULE 13G
- 8-K2026-08-05Current report (material event)
- 10-Q2026-08-05Quarterly report
- SCHEDULE 13G/A2026-07-31SCHEDULE 13G/A
- SCHEDULE 13G/A2026-07-30SCHEDULE 13G/A
- S-82026-07-28Employee stock plan
- 8-K2026-07-27Current report (material event)
- S-82026-06-04Employee stock plan
- 8-K2026-06-04Current report (material event)
- 13F-HR2026-05-1313F-HR
- 8-K2026-05-06Current report (material event)
- 10-Q2026-05-06Quarterly report
- SCHEDULE 13G2026-04-30SCHEDULE 13G
- SCHEDULE 13G2026-04-29SCHEDULE 13G
- ARS2026-04-24Annual report to holders
- DEFA14A2026-04-24DEFA14A
- DEF 14A2026-04-24Proxy statement
- SCHEDULE 13G/A2026-03-27SCHEDULE 13G/A
- 10-K2026-03-02Annual report
- 8-K2026-02-25Current report (material event)
- 8-K2026-02-25Current report (material event)
- SCHEDULE 13G2026-02-13SCHEDULE 13G
- 13F-HR2026-02-1313F-HR
- SCHEDULE 13G/A2026-01-21SCHEDULE 13G/A
- 8-K2026-01-12Current report (material event)
- 8-K2025-12-19Current report (material event)
- 8-K2025-12-11Current report (material event)
- 8-K2025-12-08Current report (material event)
- SCHEDULE 13G/A2025-11-14SCHEDULE 13G/A
- SCHEDULE 13G2025-11-10SCHEDULE 13G
- 10-Q2025-11-06Quarterly report
- 8-K2025-11-03Current report (material event)
- SCHEDULE 13G/A2025-09-08SCHEDULE 13G/A
- 8-K2025-08-29Current report (material event)
- 8-K2025-08-21Current report (material event)
- SCHEDULE 13D/A2025-08-15SCHEDULE 13D/A
- 8-K2025-08-13Current report (material event)
Source: SEC EDGAR. Forms 3/4/5 and 144 (insider transactions) are intentionally left out.